Calf cramp in children with Charcot-Marie-Tooth disease: searching for therapeutic targets

نویسندگان

  • Fiona Hawke
  • Monique Ryan
  • Robert Ouvrier
  • Joshua Burns
چکیده

Background Leg muscle cramps have been identified as the strongest independent predictor of worse quality of life in Australian children with Charcot-Marie-Tooth disease Type 1A (CMT1A). There is no accepted treatment for cramp in children with CMT and the cause of cramp is not well understood. Potential therapeutic targets should be carefully identified to direct clinical trials of interventions.

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عنوان ژورنال:

دوره 4  شماره 

صفحات  -

تاریخ انتشار 2011